The Medical Letter on Drugs and Therapeutics
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ISSUE1603
ISSUE1603
July 27, 2020
Golodirsen (Vyondys 53) for Duchenne Muscular Dystrophy
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Golodirsen (Vyondys 53) for Duchenne Muscular Dystrophy
July 27, 2020 (Issue: 1603)
Golodirsen (Vyondys 53 — Sarepta), an antisense
oligonucleotide, has received accelerated approval
from the FDA for treatment of Duchenne muscular
dystrophy (DMD) in the ~8% of patients who have
mutations of the dystrophin gene that are...more
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